FOXO3a AICD Aav10 Maternal behavior Cofilin-1 Cartilage and bone regeneration Bone development Adult SMA Intra-CSF delivery Adenosine Clinical markers Amyotrophic Lateral Sclerosis Extremely preterm infants Cell reprogramming Icv Spinal muscular atrophy CNS IPSCs Fetal growth restriction Fabry disease lysosomal storage disorders adeno asociated virus-9 Dicer ASO Coagulation factor IX Mouse model SMN Intra-uterine growth restriction MRNP assembly Inflammation Cell stemness LMNA Bone involvement Brain 3xTgAD Mice Biomarker ALS Brain development G-Secretase Calcium handling GeneRide MUNIX FTD Early-onset sepsis ASOs Genetics Adult patients Disease heterogeneity Brain injury Skeletal muscle Gene transfer Clinical trials Glucocorticosteroid Dilated cardiomyopathy Gene therapy Duchenne Muscular Dystrophy Blood brain barrier Brain imaging Brain MRI Biomarkers Maternal malnutrition Maladie neuromusculaire Modèle murin Functional outcomes IUGR Long-term handicap Melatonin DPRs MND Diseases Brain damage Mecp2 Cellules souches musculaires Biological marker Les paramètres respiratoires Microglia MiRNA Genetical therapy Distal myopathy Effector T cells Clinical trial ERK1/2 signaling Albumin gene targeting MRI Antisense oligonucleotides Prematurity Errance diagnotique Neuromuscular disease FGR Longitudinal progression IRM Amyotrophie spinale Epigenetic changes CRISPR/SaCas9 DTI C9orf72 GABA Chondrocytes Disease modifiers AAV Bioinformatics Lentiviral vectors